Tuesday, December 4, 2012

Update On Dr. Kaspar's Gene Therapy Program

This afternoon, the Recombinant DNA Advisory Committee (RAC) unanimously voted YES to Dr. Kaspar's Gene Therapy program moving forward to the FDA for final approval. This is one HUGE step forward towards curing SMA.

Thank you to everyone who continues to spread awareness about SMA and who has made and continues to make donations in Avery's name towards finding a cure for SMA!  

And a special thank you to the families who attended today's meeting.  You all brought tears to our eyes and hope to our hearts.

Don't forget to share my story by following & forwarding my blog, following me on 
Twitter  (AveryBucketList) and Like Me on Facebook (Averys Bucket List)!  The more people who are aware of SMA, the less likely future children will be diagnosed with SMA, and the more likely there will be a cure for my friends who already have SMA!


  1. WooHoo! Best news I heard all day!! xo

  2. Congrats to Avery and Avery's mommy and daddy! She would be so proud of the 2 of you for continuing to fight for her cause. Thinking of you often. God Bless from Missouri!

  3. Wonderful update, thank you for posting!

    Always in my heart, Avery...
    Xoxo, your SMAn Melissa

  4. Love the picture, soo cute! Thanks so much for sharing & I look forward to future posts! :)