The FDA has approved Dr. Kaspar's Gene Therapy program!
We would like to say thank you to Dr. Kaspar and his team at Nationwide Children's Hospital, along with Sophia's Cure Foundation and numerous other families of children with SMA for working vigorously towards making this day become a reality.
We would also like to thank everyone who followed and supported Avery and donated to Dr. Kaspar's Gene Therapy program. We hope you'll take a few minutes today or this weekend to celebrate this accomplishment while continuing to spread awareness about SMA!
Lastly and most importantly in our humbly biased opinion, we would like to give special thanks to our amazing daughter Avery for inspiring us and countless others. We ever so dearly love you and we will forever miss you.
We will finish this post with an adorable and amazing video from the Gaynor family (Founders of the Sophia's Cure Foundation) announcing the FDA's approval.